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Patient selection for hemophilia gene therapy: Real‐life data from a single center

BACKGROUND: While the number of individuals with hemophilia who are expected to be or have already been included in gene therapy trials has been regularly reported, the number of unscreened or excluded individuals, in addition to the reasons for exclusion, is mostly not reported. METHODS: We conduct...

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Detalles Bibliográficos
Autores principales: Krumb, Evelien, Lambert, Catherine, Hermans, Cedric
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8035793/
https://www.ncbi.nlm.nih.gov/pubmed/33870024
http://dx.doi.org/10.1002/rth2.12494