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Long-term follow-up of cystinosis patients treated with 0.55% cysteamine hydrochloride
BACKGROUND/AIMS: Cystinosis is a rare, autosomal recessive disorder causing defective transport of cystine out of lysosomes. Cystadrops (0.55% cysteamine hydrochloride in viscous solution) has been used on a named-patient basis to treat the accumulation of cystine crystals in the cornea in patients...
Autores principales: | , , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BMJ Publishing Group
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8077218/ https://www.ncbi.nlm.nih.gov/pubmed/32593979 http://dx.doi.org/10.1136/bjophthalmol-2020-316450 |