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Nucleic Acid–Based Therapeutics in Orphan Neurological Disorders: Recent Developments
The possibility of rational design and the resulting faster and more cost-efficient development cycles of nucleic acid–based therapeutics (NBTs), such as antisense oligonucleotides, siRNAs, and gene therapy vectors, have fueled increased activity in developing therapies for orphan diseases. Despite...
Autores principales: | , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2021
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Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8115123/ https://www.ncbi.nlm.nih.gov/pubmed/33996898 http://dx.doi.org/10.3389/fmolb.2021.643681 |