An Update on Gene Therapy for Inherited Retinal Dystrophy: Experience in Leber Congenital Amaurosis Clinical Trials

Inherited retinal dystrophies (IRDs) are a group of rare eye diseases caused by gene mutations that result in the degradation of cone and rod photoreceptors or the retinal pigment epithelium. Retinal degradation progress is often irreversible, with clinical manifestations including color or night bl...

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Detalles Bibliográficos
Autores principales: Chiu, Wei, Lin, Ting-Yi, Chang, Yun-Chia, Isahwan-Ahmad Mulyadi Lai, Henkie, Lin, Shen-Che, Ma, Chun, Yarmishyn, Aliaksandr A., Lin, Shiuan-Chen, Chang, Kao-Jung, Chou, Yu-Bai, Hsu, Chih-Chien, Lin, Tai-Chi, Chen, Shih-Jen, Chien, Yueh, Yang, Yi-Ping, Hwang, De-Kuang
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8123696/
https://www.ncbi.nlm.nih.gov/pubmed/33926102
http://dx.doi.org/10.3390/ijms22094534

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8123696/
https://www.ncbi.nlm.nih.gov/pubmed/33926102
http://dx.doi.org/10.3390/ijms22094534

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