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Newborn Screening and Treatment of Phenylketonuria: Projected Health Outcomes and Cost-Effectiveness

The objective of this study was to evaluate the cost-effectiveness of newborn screening and treatment for phenylketonuria (PKU) in the context of new data on adherence to recommended diet treatment and a newly available drug treatment (sapropterin dihydrochloride). A computer simulation model was de...

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Detalles Bibliográficos
Autores principales: Chen, Huey-Fen, Rose, Angela M., Waisbren, Susan, Ahmad, Ayesha, Prosser, Lisa A.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8151371/
https://www.ncbi.nlm.nih.gov/pubmed/34065950
http://dx.doi.org/10.3390/children8050381