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Newborn Screening and Treatment of Phenylketonuria: Projected Health Outcomes and Cost-Effectiveness
The objective of this study was to evaluate the cost-effectiveness of newborn screening and treatment for phenylketonuria (PKU) in the context of new data on adherence to recommended diet treatment and a newly available drug treatment (sapropterin dihydrochloride). A computer simulation model was de...
Autores principales: | Chen, Huey-Fen, Rose, Angela M., Waisbren, Susan, Ahmad, Ayesha, Prosser, Lisa A. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8151371/ https://www.ncbi.nlm.nih.gov/pubmed/34065950 http://dx.doi.org/10.3390/children8050381 |
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