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Targeted SMN Exon Skipping: A Useful Control to Assess In Vitro and In Vivo Splice-Switching Studies

The literature surrounding the use of antisense oligonucleotides continues to grow, with new disease and mechanistic applications constantly evolving. Furthermore, the discovery and advancement of novel chemistries continues to improve antisense delivery, stability and effectiveness. For each new ap...

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Detalles Bibliográficos
Autores principales: Flynn, Loren L., Mitrpant, Chalermchai, Adams, Abbie, Pitout, Ianthe L., Stirnweiss, Anja, Fletcher, Sue, Wilton, Steve D.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8156830/
https://www.ncbi.nlm.nih.gov/pubmed/34069072
http://dx.doi.org/10.3390/biomedicines9050552