Safety, Tolerability, and Effect of Nusinersen Treatment in Ambulatory Adults With 5q-SMA

Objective: To determine the safety and tolerability of nusinersen treatment in ambulatory adults with spinal muscular atrophy (SMA) and investigate the treatment effect on muscle strength, physical function, and motor unit physiology. Methods: Individuals aged 18 years or older with genetically conf...

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Detalles Bibliográficos
Autores principales: Elsheikh, Bakri, Severyn, Steven, Zhao, Songzhu, Kline, David, Linsenmayer, Matthew, Kelly, Kristina, Tellez, Marco, Bartlett, Amy, Heintzman, Sarah, Reynolds, Jerry, Sterling, Gary, Weaver, Tristan, Rajneesh, Kiran, Kolb, Stephen J., Arnold, W. David
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2021
Materias:
Neurology
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8174580/
https://www.ncbi.nlm.nih.gov/pubmed/34093395
http://dx.doi.org/10.3389/fneur.2021.650535

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8174580/
https://www.ncbi.nlm.nih.gov/pubmed/34093395
http://dx.doi.org/10.3389/fneur.2021.650535

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