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A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells

Chinese hamster ovary (CHO) cells are the most widely used host for the expression of therapeutic proteins. Recently, significant progress has been made due to advances in genome sequence and annotation quality to unravel the black box CHO. Nevertheless, in many cases the link between genotype and p...

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Autores principales: Schmieder, Valerie, Novak, Neža, Dhiman, Heena, Nguyen, Ly Ngoc, Serafimova, Evgenija, Klanert, Gerald, Baumann, Martina, Kildegaard, Helene Faustrup, Borth, Nicole
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8261548/
https://www.ncbi.nlm.nih.gov/pubmed/34277363
http://dx.doi.org/10.1016/j.btre.2021.e00649
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author Schmieder, Valerie
Novak, Neža
Dhiman, Heena
Nguyen, Ly Ngoc
Serafimova, Evgenija
Klanert, Gerald
Baumann, Martina
Kildegaard, Helene Faustrup
Borth, Nicole
author_facet Schmieder, Valerie
Novak, Neža
Dhiman, Heena
Nguyen, Ly Ngoc
Serafimova, Evgenija
Klanert, Gerald
Baumann, Martina
Kildegaard, Helene Faustrup
Borth, Nicole
author_sort Schmieder, Valerie
collection PubMed
description Chinese hamster ovary (CHO) cells are the most widely used host for the expression of therapeutic proteins. Recently, significant progress has been made due to advances in genome sequence and annotation quality to unravel the black box CHO. Nevertheless, in many cases the link between genotype and phenotype in the context of suspension cultivated production cell lines is still not fully understood. While frameshift approaches targeting coding genes are frequently used, the non-coding regions of the genome have received less attention with respect to such functional annotation. Importantly, for non-coding regions frameshift knock-out strategies are not feasible. In this study, we developed a CRISPR-mediated screening approach that performs full deletions of genomic regions to enable the functional study of both the translated and untranslated genome. An in silico pipeline for the computational high-throughput design of paired guide RNAs (pgRNAs) directing CRISPR/AsCpf1 was established and used to generate a library tackling process-related genes and long non-coding RNAs. Next generation sequencing analysis of the plasmid library revealed a sufficient, but highly variable pgRNA composition. Recombinase-mediated cassette exchange was applied for pgRNA library integration rather than viral transduction to ensure single copy representation of pgRNAs per cell. After transient AsCpf1 expression, cells were cultivated over two sequential batches to identify pgRNAs which massively affected growth and survival. By comparing pgRNA abundance, depleted candidates were identified and individually validated to verify their effect.
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spelling pubmed-82615482021-07-16 A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells Schmieder, Valerie Novak, Neža Dhiman, Heena Nguyen, Ly Ngoc Serafimova, Evgenija Klanert, Gerald Baumann, Martina Kildegaard, Helene Faustrup Borth, Nicole Biotechnol Rep (Amst) Research Article Chinese hamster ovary (CHO) cells are the most widely used host for the expression of therapeutic proteins. Recently, significant progress has been made due to advances in genome sequence and annotation quality to unravel the black box CHO. Nevertheless, in many cases the link between genotype and phenotype in the context of suspension cultivated production cell lines is still not fully understood. While frameshift approaches targeting coding genes are frequently used, the non-coding regions of the genome have received less attention with respect to such functional annotation. Importantly, for non-coding regions frameshift knock-out strategies are not feasible. In this study, we developed a CRISPR-mediated screening approach that performs full deletions of genomic regions to enable the functional study of both the translated and untranslated genome. An in silico pipeline for the computational high-throughput design of paired guide RNAs (pgRNAs) directing CRISPR/AsCpf1 was established and used to generate a library tackling process-related genes and long non-coding RNAs. Next generation sequencing analysis of the plasmid library revealed a sufficient, but highly variable pgRNA composition. Recombinase-mediated cassette exchange was applied for pgRNA library integration rather than viral transduction to ensure single copy representation of pgRNAs per cell. After transient AsCpf1 expression, cells were cultivated over two sequential batches to identify pgRNAs which massively affected growth and survival. By comparing pgRNA abundance, depleted candidates were identified and individually validated to verify their effect. Elsevier 2021-06-20 /pmc/articles/PMC8261548/ /pubmed/34277363 http://dx.doi.org/10.1016/j.btre.2021.e00649 Text en © 2021 Published by Elsevier B.V. https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
spellingShingle Research Article
Schmieder, Valerie
Novak, Neža
Dhiman, Heena
Nguyen, Ly Ngoc
Serafimova, Evgenija
Klanert, Gerald
Baumann, Martina
Kildegaard, Helene Faustrup
Borth, Nicole
A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title_full A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title_fullStr A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title_full_unstemmed A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title_short A pooled CRISPR/AsCpf1 screen using paired gRNAs to induce genomic deletions in Chinese hamster ovary cells
title_sort pooled crispr/ascpf1 screen using paired grnas to induce genomic deletions in chinese hamster ovary cells
topic Research Article
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8261548/
https://www.ncbi.nlm.nih.gov/pubmed/34277363
http://dx.doi.org/10.1016/j.btre.2021.e00649
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