Capturing Data in Rare Disease Registries to Support Regulatory Decision Making: A Survey Study Among Industry and Other Stakeholders

INTRODUCTION: In rare diseases, registry-based studies can be used to provide natural history data pre-approval and complement drug efficacy and/or safety knowledge post-approval. OBJECTIVE: The objective of this study was to investigate the opinion of stakeholders about key aspects of rare disease...

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Detalles Bibliográficos
Autores principales: Jonker, Carla J., de Vries, Sieta T., van den Berg, H. Marijke, McGettigan, Patricia, Hoes, Arno W., Mol, Peter G. M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2021
Materias:
Original Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8279983/
https://www.ncbi.nlm.nih.gov/pubmed/34091881
http://dx.doi.org/10.1007/s40264-021-01081-z

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8279983/
https://www.ncbi.nlm.nih.gov/pubmed/34091881
http://dx.doi.org/10.1007/s40264-021-01081-z

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