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The Use of Patient-Reported Outcome Measures in Rare Diseases and Implications for Health Technology Assessment

BACKGROUND: Patient-reported outcome measures (PROMs) are used in health technology assessment (HTA) to measure patient experiences with disease and treatment, allowing a deeper understanding of treatment impact beyond clinical endpoints. Developing and administering PROMs for rare diseases poses un...

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Detalles Bibliográficos
Autores principales:	Whittal, Amanda, Meregaglia, Michela, Nicod, Elena
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer International Publishing 2021
Materias:	Review Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8357707/ https://www.ncbi.nlm.nih.gov/pubmed/33462774 http://dx.doi.org/10.1007/s40271-020-00493-w

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