Cargando…

Rare Genetic Disorders: Novel Treatment Strategies and Insights Into Human Biology

The last decade has seen a dramatic increase in innovative ideas for the treatment of genetic disorders for which no curative therapies exist. Gene and protein replacement therapies stand out as novel approaches to treat a select group of these diseases, such as certain tissue fragility disorders. F...

Descripción completa

Detalles Bibliográficos
Autores principales: Koch, Peter J., Koster, Maranke I.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8378213/
https://www.ncbi.nlm.nih.gov/pubmed/34422015
http://dx.doi.org/10.3389/fgene.2021.714764