Novel Severe Hemophilia A Mouse Model with Factor VIII Intron 22 Inversion

SIMPLE SUMMARY: Recently, innovative gene therapy has been developing toward functional restoration by gain of function or gene correction. Hemophilia is a representative genetic disorder with many human patients and is considered a candidate disease for gene therapy. The most frequent severe hemoph...

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Detalles Bibliográficos
Autores principales: Han, Jeong Pil, Song, Dong Woo, Lee, Jeong Hyeon, Lee, Geon Seong, Yeom, Su Cheong
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Communication
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8389204/
https://www.ncbi.nlm.nih.gov/pubmed/34439937
http://dx.doi.org/10.3390/biology10080704

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8389204/
https://www.ncbi.nlm.nih.gov/pubmed/34439937
http://dx.doi.org/10.3390/biology10080704

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