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The intersection of vector biology, gene therapy, and hemophilia
Gene therapy is at the forefront of the drive to bring the potential of cure to patients with genetic diseases. Multiple mechanisms of effective and efficient gene therapy delivery (eg, lentiviral, adeno‐associated) for transgene expression as well as gene editing have been explored to improve vecto...
Autores principales: | , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8410952/ https://www.ncbi.nlm.nih.gov/pubmed/34485808 http://dx.doi.org/10.1002/rth2.12586 |