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The intersection of vector biology, gene therapy, and hemophilia

Gene therapy is at the forefront of the drive to bring the potential of cure to patients with genetic diseases. Multiple mechanisms of effective and efficient gene therapy delivery (eg, lentiviral, adeno‐associated) for transgene expression as well as gene editing have been explored to improve vecto...

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Detalles Bibliográficos
Autores principales: Lisowski, Leszek, Staber, Janice M., Wright, J. Fraser, Valentino, Leonard A.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8410952/
https://www.ncbi.nlm.nih.gov/pubmed/34485808
http://dx.doi.org/10.1002/rth2.12586