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Current Pharmacological Strategies for Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is a lethal, X-linked neuromuscular disorder caused by the absence of dystrophin protein, which is essential for muscle fiber integrity. Loss of dystrophin protein leads to recurrent myofiber damage, chronic inflammation, progressive fibrosis, and dysfunction of mus...

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Detalles Bibliográficos
Autores principales: Yao, Shanshan, Chen, Zihao, Yu, Yuanyuan, Zhang, Ning, Jiang, Hewen, Zhang, Ge, Zhang, Zongkang, Zhang, Baoting
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8417245/
https://www.ncbi.nlm.nih.gov/pubmed/34490244
http://dx.doi.org/10.3389/fcell.2021.689533