Nusinersen for Spinal Muscular Atrophy in the United States: Findings From a Retrospective Claims Database Analysis

INTRODUCTION: Spinal muscular atrophy (SMA) is a rare, genetic neuromuscular disorder caused by deletion/mutation of the survival motor neuron 1 gene, characterized by progressive loss of motor neurons, resulting in increasing muscular weakness, deteriorating motor function, and, in its most severe...

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Detalles Bibliográficos
Autores principales: Gauthier-Loiselle, Marjolaine, Cloutier, Martin, Toro, Walter, Patel, Anish, Shi, Sherry, Davidson, Mikhail, Bischof, Matthias, LaMarca, Nicole, Dabbous, Omar
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Healthcare 2021
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8552979/
https://www.ncbi.nlm.nih.gov/pubmed/34713391
http://dx.doi.org/10.1007/s12325-021-01938-w

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8552979/
https://www.ncbi.nlm.nih.gov/pubmed/34713391
http://dx.doi.org/10.1007/s12325-021-01938-w

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