Gene Therapies for Monogenic Autism Spectrum Disorders

Novel genome editing and transient gene therapies have been developed the past ten years, resulting in the first in-human clinical trials for monogenic disorders. Syndromic autism spectrum disorders can be caused by mutations in a single gene. Given the monogenic aspect and severity of syndromic ASD...

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Detalles Bibliográficos
Autores principales: Weuring, Wout, Geerligs, Jeroen, Koeleman, Bobby P. C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8617899/
https://www.ncbi.nlm.nih.gov/pubmed/34828273
http://dx.doi.org/10.3390/genes12111667

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8617899/
https://www.ncbi.nlm.nih.gov/pubmed/34828273
http://dx.doi.org/10.3390/genes12111667

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