Burden of cystic fibrosis in children <12 years of age prior to the introduction of CFTR modulator therapies

BACKGROUND: Cystic fibrosis (CF) is a genetic, multisystemic, progressive and life-shortening disease caused by mutations in the CF transmembrane conductance regulator (CFTR) gene. Different genotypes have been linked to variations in disease progression among people with CF. The burden of illness (...

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Detalles Bibliográficos
Autores principales: Bresnick, Kathryn, Arteaga-Solis, Emilio, Millar, Stefanie J, Laird, Glen, LeCamus, Cecile
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BMJ Publishing Group 2021
Materias:
Cystic Fibrosis
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8640656/
https://www.ncbi.nlm.nih.gov/pubmed/34857524
http://dx.doi.org/10.1136/bmjresp-2021-000998

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8640656/
https://www.ncbi.nlm.nih.gov/pubmed/34857524
http://dx.doi.org/10.1136/bmjresp-2021-000998

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