Clinical development innovation in rare diseases: lessons learned and best practices from the DevelopAKUre consortium

New opportunities have arisen for development of therapies for rare diseases with the increased focus and progress in the field. However, standardised framework integrating individual initiatives has not been formed. We present lessons learned and best practice from a collaborative success case in d...

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Detalles Bibliográficos
Autores principales: Rudebeck, Mattias, Scott, Ciarán, Rhodes, Nicholas P., van Kan, Christa, Olsson, Birgitta, Al-sbou, Mohammed, Hall, Anthony K., Sireau, Nicolas, Ranganath, Lakshminarayan R.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2021
Materias:
Position Statement
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8670024/
https://www.ncbi.nlm.nih.gov/pubmed/34906169
http://dx.doi.org/10.1186/s13023-021-02137-0

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8670024/
https://www.ncbi.nlm.nih.gov/pubmed/34906169
http://dx.doi.org/10.1186/s13023-021-02137-0

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