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The Minimal Clinical Important Difference (MCID) in Annual Rate of Change of Timed Function Tests in Boys with DMD

BACKGROUND: Duchenne muscular dystrophy (DMD) is a rare x-linked recessive genetic disorder affecting 1 in every 5000–10000 [1, 2]. This disease leads to a variable but progressive sequential pattern of muscle weakness that eventually causes loss of important functional milestones such as the abilit...

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Detalles Bibliográficos
Autores principales: Duong, Tina, Canbek, Jennifer, Birkmeier, Marisa, Nelson, Leslie, Siener, Catherine, Fernandez-Fernandez, Alicia, Henricson, Erik, McDonald, Craig M., Gordish-Dressman, Heather
Formato: Online Artículo Texto
Lenguaje:English
Publicado: IOS Press 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8673528/
https://www.ncbi.nlm.nih.gov/pubmed/34151852
http://dx.doi.org/10.3233/JND-210646