Targeted Therapies for Leigh Syndrome: Systematic Review and Steps Towards a ‘Treatabolome’

BACKGROUND: Leigh syndrome (LS) is the most frequent paediatric clinical presentation of mitochondrial disease. The clinical phenotype of LS is highly heterogeneous. Though historically the treatment for LS is largely supportive, new treatments are on the horizon. Due to the rarity of LS, large-scal...

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Detalles Bibliográficos
Autores principales: Tiet, May Yung, Lin, Zhiyuan, Gao, Fei, Jennings, Matthew James, Horvath, Rita
Formato: Online Artículo Texto
Lenguaje:English
Publicado: IOS Press 2021
Materias:
Research Report
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8673543/
https://www.ncbi.nlm.nih.gov/pubmed/34308912
http://dx.doi.org/10.3233/JND-210715

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8673543/
https://www.ncbi.nlm.nih.gov/pubmed/34308912
http://dx.doi.org/10.3233/JND-210715

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