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Emerging Oligonucleotide Therapeutics for Rare Neuromuscular Diseases

Research and drug development concerning rare diseases are at the cutting edge of scientific technology. To date, over 7,000 rare diseases have been identified. Despite their individual rarity, 1 in 10 individuals worldwide is affected by a rare condition. For the majority of these diseases, there i...

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Detalles Bibliográficos
Autores principales: Aoki, Yoshitsugu, Wood, Matthew J.A.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: IOS Press 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8673547/
https://www.ncbi.nlm.nih.gov/pubmed/34092651
http://dx.doi.org/10.3233/JND-200560