Prediction of Real-World Long-Term Outcomes of People with CF Homozygous for the F508del Mutation Treated with CFTR Modulators

The clinical response to cystic fibrosis transmembrane conductance regulator (CFTR) modulators is variable within people with cystic fibrosis (pwCF) homozygous for the F508del mutation. The prediction of clinical effect in individual patients would be useful to target therapy to those who would bene...

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Detalles Bibliográficos
Autores principales: Muilwijk, Danya, Bierlaagh, Marlou, van Mourik, Peter, Kraaijkamp, Jasmijn, van der Meer, Renske, van den Bor, Rutger, Heijerman, Harry, Eijkemans, René, Beekman, Jeffrey, van der Ent, Kors
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8707616/
https://www.ncbi.nlm.nih.gov/pubmed/34945848
http://dx.doi.org/10.3390/jpm11121376

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8707616/
https://www.ncbi.nlm.nih.gov/pubmed/34945848
http://dx.doi.org/10.3390/jpm11121376

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