Responder analysis for neuropathic impairment and quality-of-life assessment in patients with hereditary transthyretin amyloidosis with polyneuropathy in the NEURO-TTR study

OBJECTIVE: Hereditary transthyretin amyloidosis with polyneuropathy (ATTRv-PN) is a rare disease characterized by rapid neuropathic progression. In pivotal studies of gene-silencing treatments, the modified Neuropathy Impairment Score + 7 tests (mNIS + 7) and Norfolk-Quality of Life (QOL)-Diabetic N...

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Detalles Bibliográficos
Autores principales: Yarlas, Aaron, Lovley, Andrew, Brown, Duncan, Kosinski, Mark, Vera-Llonch, Montserrat
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Berlin Heidelberg 2021
Materias:
Original Communication
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8739287/
https://www.ncbi.nlm.nih.gov/pubmed/34125267
http://dx.doi.org/10.1007/s00415-021-10635-1

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8739287/
https://www.ncbi.nlm.nih.gov/pubmed/34125267
http://dx.doi.org/10.1007/s00415-021-10635-1

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