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Chronic lithium administration in a mouse model for Krabbe disease

Krabbe disease (KD; or globoid cell leukodystrophy) is an autosomal recessive lysosomal storage disorder caused by deficiency of the galactosylceramidase (GALC) enzyme. No cure is currently available for KD. Clinical applied treatments are supportive only. Recently, we demonstrated that two differen...

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Detalles Bibliográficos
Autores principales: Del Grosso, Ambra, Parlanti, Gabriele, Angella, Lucia, Giordano, Nadia, Tonazzini, Ilaria, Ottalagana, Elisa, Carpi, Sara, Pellegrino, Roberto Maria, Alabed, Husam B. R., Emiliani, Carla, Caleo, Matteo, Cecchini, Marco
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley & Sons, Inc. 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8743347/
https://www.ncbi.nlm.nih.gov/pubmed/35028271
http://dx.doi.org/10.1002/jmd2.12258