Nucleic Acid-Based Therapeutic Approach for Spinal and Bulbar Muscular Atrophy and Related Neurological Disorders

The recent advances in nucleic acid therapeutics demonstrate the potential to treat hereditary neurological disorders by targeting their causative genes. Spinal and bulbar muscular atrophy (SBMA) is an X-linked and adult-onset neurodegenerative disorder caused by the expansion of trinucleotide cytos...

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Detalles Bibliográficos
Autores principales: Hirunagi, Tomoki, Sahashi, Kentaro, Meilleur, Katherine G., Katsuno, Masahisa
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8775157/
https://www.ncbi.nlm.nih.gov/pubmed/35052449
http://dx.doi.org/10.3390/genes13010109

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8775157/
https://www.ncbi.nlm.nih.gov/pubmed/35052449
http://dx.doi.org/10.3390/genes13010109

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