Gene-Based Therapeutics for Inherited Retinal Diseases

Inherited retinal diseases (IRDs) are a heterogenous group of orphan eye diseases that typically result from monogenic mutations and are considered attractive targets for gene-based therapeutics. Following the approval of an IRD gene replacement therapy for Leber’s congenital amaurosis due to RPE65...

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Detalles Bibliográficos
Autores principales: Fenner, Beau J., Tan, Tien-En, Barathi, Amutha Veluchamy, Tun, Sai Bo Bo, Yeo, Sia Wey, Tsai, Andrew S. H., Lee, Shu Yen, Cheung, Chui Ming Gemmy, Chan, Choi Mun, Mehta, Jodhbir S., Teo, Kelvin Y. C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2022
Materias:
Genetics
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8782148/
https://www.ncbi.nlm.nih.gov/pubmed/35069693
http://dx.doi.org/10.3389/fgene.2021.794805

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8782148/
https://www.ncbi.nlm.nih.gov/pubmed/35069693
http://dx.doi.org/10.3389/fgene.2021.794805

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