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Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine

Lipid nanoparticle (LNP)-formulated nucleoside-modified mRNA vaccines have proven to be very successful in the fight against the coronavirus disease 2019 (COVID-19) pandemic. They are effective, safe, and can be produced in large quantities. However, the long-term storage of mRNA-LNP vaccines withou...

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Autores principales: Muramatsu, Hiromi, Lam, Kieu, Bajusz, Csaba, Laczkó, Dorottya, Karikó, Katalin, Schreiner, Petra, Martin, Alan, Lutwyche, Peter, Heyes, James, Pardi, Norbert
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Gene & Cell Therapy 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8815268/
https://www.ncbi.nlm.nih.gov/pubmed/35131437
http://dx.doi.org/10.1016/j.ymthe.2022.02.001
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author Muramatsu, Hiromi
Lam, Kieu
Bajusz, Csaba
Laczkó, Dorottya
Karikó, Katalin
Schreiner, Petra
Martin, Alan
Lutwyche, Peter
Heyes, James
Pardi, Norbert
author_facet Muramatsu, Hiromi
Lam, Kieu
Bajusz, Csaba
Laczkó, Dorottya
Karikó, Katalin
Schreiner, Petra
Martin, Alan
Lutwyche, Peter
Heyes, James
Pardi, Norbert
author_sort Muramatsu, Hiromi
collection PubMed
description Lipid nanoparticle (LNP)-formulated nucleoside-modified mRNA vaccines have proven to be very successful in the fight against the coronavirus disease 2019 (COVID-19) pandemic. They are effective, safe, and can be produced in large quantities. However, the long-term storage of mRNA-LNP vaccines without freezing is still a challenge. Here, we demonstrate that nucleoside-modified mRNA-LNPs can be lyophilized, and the physicochemical properties of the lyophilized material do not significantly change for 12 weeks after storage at room temperature and for at least 24 weeks after storage at 4°C. Importantly, we show in comparative mouse studies that lyophilized firefly luciferase-encoding mRNA-LNPs maintain their high expression, and no decrease in the immunogenicity of a lyophilized influenza virus hemagglutinin-encoding mRNA-LNP vaccine was observed after 12 weeks of storage at room temperature or for at least 24 weeks after storage at 4°C. Our studies offer a potential solution to overcome the long-term storage-related limitations of nucleoside-modified mRNA-LNP vaccines.
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spelling pubmed-88152682022-02-04 Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine Muramatsu, Hiromi Lam, Kieu Bajusz, Csaba Laczkó, Dorottya Karikó, Katalin Schreiner, Petra Martin, Alan Lutwyche, Peter Heyes, James Pardi, Norbert Mol Ther Original Article Lipid nanoparticle (LNP)-formulated nucleoside-modified mRNA vaccines have proven to be very successful in the fight against the coronavirus disease 2019 (COVID-19) pandemic. They are effective, safe, and can be produced in large quantities. However, the long-term storage of mRNA-LNP vaccines without freezing is still a challenge. Here, we demonstrate that nucleoside-modified mRNA-LNPs can be lyophilized, and the physicochemical properties of the lyophilized material do not significantly change for 12 weeks after storage at room temperature and for at least 24 weeks after storage at 4°C. Importantly, we show in comparative mouse studies that lyophilized firefly luciferase-encoding mRNA-LNPs maintain their high expression, and no decrease in the immunogenicity of a lyophilized influenza virus hemagglutinin-encoding mRNA-LNP vaccine was observed after 12 weeks of storage at room temperature or for at least 24 weeks after storage at 4°C. Our studies offer a potential solution to overcome the long-term storage-related limitations of nucleoside-modified mRNA-LNP vaccines. American Society of Gene & Cell Therapy 2022-05-04 2022-02-04 /pmc/articles/PMC8815268/ /pubmed/35131437 http://dx.doi.org/10.1016/j.ymthe.2022.02.001 Text en © 2022 The Author(s) https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
spellingShingle Original Article
Muramatsu, Hiromi
Lam, Kieu
Bajusz, Csaba
Laczkó, Dorottya
Karikó, Katalin
Schreiner, Petra
Martin, Alan
Lutwyche, Peter
Heyes, James
Pardi, Norbert
Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title_full Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title_fullStr Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title_full_unstemmed Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title_short Lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mRNA vaccine
title_sort lyophilization provides long-term stability for a lipid nanoparticle-formulated, nucleoside-modified mrna vaccine
topic Original Article
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8815268/
https://www.ncbi.nlm.nih.gov/pubmed/35131437
http://dx.doi.org/10.1016/j.ymthe.2022.02.001
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