REAL‐world clinical effectiveness of ivacaftor therapy in the first 24 months in two infants with cystic fibrosis and different gating mutations—A case report

This study summarizes efficacy of ivacaftor treatment in 2 infants in a real‐world setting. A distinct decline of sweat chloride and lung clearance index plus increase in fecal elastase was seen. The results underline the early and sustainable effect and give cause for discussing whether a reduction...

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Detalles Bibliográficos
Autores principales: Fuchs, Teresa, Appelt, Dorothea, Niedermayr, Katharina, Ellemunter, Helmut
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2022
Materias:
Case Reports
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8829656/
https://www.ncbi.nlm.nih.gov/pubmed/35154718
http://dx.doi.org/10.1002/ccr3.5364

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8829656/
https://www.ncbi.nlm.nih.gov/pubmed/35154718
http://dx.doi.org/10.1002/ccr3.5364

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