Difficulties Associated with Enzyme Replacement Therapy for Mucopolysaccharidoses

BACKGROUND: Mucopolysaccharidoses are extremely rare, progressive, often severe multisystem disorders, some of which are managed by weekly intravenous enzyme replacement therapy. This study aimed to determine the difficulties faced by the patients with mucopolysaccharidosis and their families due to...

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Detalles Bibliográficos
Autores principales: Yıldız, Yılmaz, Sivri, H. Serap
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Turkish Pediatrics Association 2021
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8849081/
https://www.ncbi.nlm.nih.gov/pubmed/35110060
http://dx.doi.org/10.5152/TurkArchPediatr.2021.21235

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8849081/
https://www.ncbi.nlm.nih.gov/pubmed/35110060
http://dx.doi.org/10.5152/TurkArchPediatr.2021.21235

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