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Difficulties Associated with Enzyme Replacement Therapy for Mucopolysaccharidoses
BACKGROUND: Mucopolysaccharidoses are extremely rare, progressive, often severe multisystem disorders, some of which are managed by weekly intravenous enzyme replacement therapy. This study aimed to determine the difficulties faced by the patients with mucopolysaccharidosis and their families due to...
| Autores principales: | , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Turkish Pediatrics Association
2021
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8849081/ https://www.ncbi.nlm.nih.gov/pubmed/35110060 http://dx.doi.org/10.5152/TurkArchPediatr.2021.21235 |