Cargando…
Gene Therapy Advances: A Meta-Analysis of AAV Usage in Clinical Settings
Adeno-associated viruses (AAVs) are the safest and most effective gene delivery vehicles to drive long-term transgene expression in gene therapy. While animal studies have shown promising results, the translatability of AAVs into clinical settings has been partly limited due to their restricted gene...
Autores principales: | Au, Hau Kiu Edna, Isalan, Mark, Mielcarek, Michal |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2022
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8864161/ https://www.ncbi.nlm.nih.gov/pubmed/35223884 http://dx.doi.org/10.3389/fmed.2021.809118 |
Ejemplares similares
-
A minimal region of the HSP90AB1 promoter is suitable for ubiquitous expression in different somatic tissues with applicability for gene therapy
por: Mielcarek, Michal, et al.
Publicado: (2023) -
Prevalence of Non-psychiatric Comorbidities in Pre-symptomatic and Symptomatic Huntington's Disease Gene Carriers in Poland
por: Zielonka, Daniel, et al.
Publicado: (2020) -
A shared mechanism of muscle wasting in cancer and Huntington’s disease
por: Mielcarek, Michal, et al.
Publicado: (2015) -
Kinetin stimulates differentiation of C2C12 myoblasts
por: Mielcarek, Michal, et al.
Publicado: (2021) -
Polyglutamine diseases: looking beyond the neurodegenerative universe
por: Mielcarek, Michal, et al.
Publicado: (2020)