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Outcome Measures in Facioscapulohumeral Muscular Dystrophy Clinical Trials

Facioscapulohumeral muscular dystrophy (FSHD) is a debilitating muscular dystrophy with a variable age of onset, severity, and progression. While there is still no cure for this disease, progress towards FSHD therapies has accelerated since the underlying mechanism of epigenetic derepression of the...

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Detalles Bibliográficos
Autores principales: Ghasemi, Mehdi, Emerson, Charles P., Hayward, Lawrence J.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8870318/
https://www.ncbi.nlm.nih.gov/pubmed/35203336
http://dx.doi.org/10.3390/cells11040687