Development of a model‐based clinical trial simulation platform to optimize the design of clinical trials for Duchenne muscular dystrophy

Early clinical trials of therapies to treat Duchenne muscular dystrophy (DMD), a fatal genetic X‐linked pediatric disease, have been designed based on the limited understanding of natural disease progression and variability in clinical measures over different stages of the continuum of the disease....

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Detalles Bibliográficos
Autores principales: Lingineni, Karthik, Aggarwal, Varun, Morales, Juan Francisco, Conrado, Daniela J., Corey, Diane, Vong, Camille, Burton, Jackson, Larkindale, Jane, Romero, Klaus, Schmidt, Stephan, Kim, Sarah
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2022
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8923721/
https://www.ncbi.nlm.nih.gov/pubmed/34877803
http://dx.doi.org/10.1002/psp4.12753

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8923721/
https://www.ncbi.nlm.nih.gov/pubmed/34877803
http://dx.doi.org/10.1002/psp4.12753

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