Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis

BACKGROUND: Duchenne muscular dystrophy (DMD) is a rare, severely debilitating, and fatal neuromuscular disease characterized by progressive muscle degeneration. Like in many orphan diseases, randomized controlled trials are uncommon in DMD, resulting in the need to indirectly compare treatment effe...

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Detalles Bibliográficos
Autores principales: Ferizovic, Nermina, Summers, Jessica, de Zárate, Igor Beitia Ortiz, Werner, Christian, Jiang, Joel, Landfeldt, Erik, Buesch, Katharina
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2022
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8956179/
https://www.ncbi.nlm.nih.gov/pubmed/35333888
http://dx.doi.org/10.1371/journal.pone.0265879

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8956179/
https://www.ncbi.nlm.nih.gov/pubmed/35333888
http://dx.doi.org/10.1371/journal.pone.0265879

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