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Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis
BACKGROUND: Duchenne muscular dystrophy (DMD) is a rare, severely debilitating, and fatal neuromuscular disease characterized by progressive muscle degeneration. Like in many orphan diseases, randomized controlled trials are uncommon in DMD, resulting in the need to indirectly compare treatment effe...
| Autores principales: | , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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Public Library of Science
2022
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8956179/ https://www.ncbi.nlm.nih.gov/pubmed/35333888 http://dx.doi.org/10.1371/journal.pone.0265879 |