Hurdles to the Adoption of Gene Therapy as a Curative Option for Transfusion-Dependent Thalassemia

Beta-thalassemia is one of the most common monogenic disorders. Standard treatment of the most severe forms, i.e., transfusion-dependent thalassemia (TDT) with long-term transfusion and iron chelation, represents a considerable medical, psychological, and economic burden. Allogeneic hematopoietic st...

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Detalles Bibliográficos
Autores principales: Thuret, Isabelle, Ruggeri, Annalisa, Angelucci, Emanuele, Chabannon, Christian
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Oxford University Press 2022
Materias:
Tissue-Specific Progenitor and Stem Cells
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9052404/
https://www.ncbi.nlm.nih.gov/pubmed/35267028
http://dx.doi.org/10.1093/stcltm/szac007

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9052404/
https://www.ncbi.nlm.nih.gov/pubmed/35267028
http://dx.doi.org/10.1093/stcltm/szac007

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