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Therapeutic opportunities and clinical outcome measures in Duchenne muscular dystrophy

INTRODUCTION: Duchenne muscular dystrophy (DMD) is a devastatingly severe genetic muscle disease characterized by childhood-onset muscle weakness, leading to loss of motor function and premature death due to respiratory and cardiac insufficiency. DISCUSSION: In the following three and half decades,...

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Detalles Bibliográficos
Autores principales: Ricci, Giulia, Bello, Luca, Torri, Francesca, Schirinzi, Erika, Pegoraro, Elena, Siciliano, Gabriele
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9126754/
https://www.ncbi.nlm.nih.gov/pubmed/35608735
http://dx.doi.org/10.1007/s10072-022-06085-w