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Development of Therapeutic RNA Manipulation for Muscular Dystrophy

Approval of therapeutic RNA molecules, including RNA vaccines, has paved the way for next-generation treatment strategies for various diseases. Oligonucleotide-based therapeutics hold particular promise for treating incurable muscular dystrophies, including Duchenne muscular dystrophy (DMD). DMD is...

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Detalles Bibliográficos
Autores principales: Saifullah, Motohashi, Norio, Tsukahara, Toshifumi, Aoki, Yoshitsugu
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9127466/
https://www.ncbi.nlm.nih.gov/pubmed/35620642
http://dx.doi.org/10.3389/fgeed.2022.863651