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In Vitro CRISPR/Cas9 Transfection and Gene-Editing Mediated by Multivalent Cationic Liposome–DNA Complexes
Clustered regularly interspaced short palindromic repeats (CRISPR) and CRISPR-associated nuclease 9 (Cas9) gene-editing offers exciting new therapeutic possibilities for disease treatment with a genetic etiology such as cancer, cardiovascular, neuronal, and immune disorders. However, its clinical tr...
Autores principales: | Sousa, Diana A., Gaspar, Ricardo, Ferreira, Celso J. O., Baltazar, Fátima, Rodrigues, Ligia R., Silva, Bruno F. B. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9143451/ https://www.ncbi.nlm.nih.gov/pubmed/35631673 http://dx.doi.org/10.3390/pharmaceutics14051087 |
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