Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses Example

Over recent decades, the many functions of RNA have become more evident. This molecule has been recognized not only as a carrier of genetic information, but also as a specific and essential regulator of gene expression. Different RNA species have been identified and novel and exciting roles have bee...

Descripción completa

Detalles Bibliográficos
Autores principales: Santos, Juliana Inês, Gonçalves, Mariana, Matos, Liliana, Moreira, Luciana, Carvalho, Sofia, Prata, Maria João, Coutinho, Maria Francisca, Alves, Sandra
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9146820/
https://www.ncbi.nlm.nih.gov/pubmed/35629276
http://dx.doi.org/10.3390/life12050608

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9146820/
https://www.ncbi.nlm.nih.gov/pubmed/35629276
http://dx.doi.org/10.3390/life12050608

Ejemplares similares