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Orphan Drug Use in Patients With Rare Diseases: A Population-Based Cohort Study

Background: Orphan drugs are used for the diagnosis, prevention and treatment of rare diseases that, in the European Union, are defined as disorders affecting no more than 5 persons in 10,000. So far, a total of around 800 orphan medicinal products have been approved by the European Medicines Agency...

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Detalles Bibliográficos
Autores principales: Gorini, Francesca, Santoro, Michele, Pierini, Anna, Mezzasalma, Lorena, Baldacci, Silvia, Bargagli, Elena, Boncristiano, Alessandra, Brunetto, Maurizia Rossana, Cameli, Paolo, Cappelli, Francesco, Castaman, Giancarlo, Coco, Barbara, Donati, Maria Alice, Guerrini, Renzo, Linari, Silvia, Murro, Vittoria, Olivotto, Iacopo, Parronchi, Paola, Pochiero, Francesca, Rossi, Oliviero, Scappini, Barbara, Sodi, Andrea, Vannucchi, Alessandro Maria, Coi, Alessio
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9148958/
https://www.ncbi.nlm.nih.gov/pubmed/35652051
http://dx.doi.org/10.3389/fphar.2022.869842