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Orphan Drug Use in Patients With Rare Diseases: A Population-Based Cohort Study
Background: Orphan drugs are used for the diagnosis, prevention and treatment of rare diseases that, in the European Union, are defined as disorders affecting no more than 5 persons in 10,000. So far, a total of around 800 orphan medicinal products have been approved by the European Medicines Agency...
Autores principales: | Gorini, Francesca, Santoro, Michele, Pierini, Anna, Mezzasalma, Lorena, Baldacci, Silvia, Bargagli, Elena, Boncristiano, Alessandra, Brunetto, Maurizia Rossana, Cameli, Paolo, Cappelli, Francesco, Castaman, Giancarlo, Coco, Barbara, Donati, Maria Alice, Guerrini, Renzo, Linari, Silvia, Murro, Vittoria, Olivotto, Iacopo, Parronchi, Paola, Pochiero, Francesca, Rossi, Oliviero, Scappini, Barbara, Sodi, Andrea, Vannucchi, Alessandro Maria, Coi, Alessio |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9148958/ https://www.ncbi.nlm.nih.gov/pubmed/35652051 http://dx.doi.org/10.3389/fphar.2022.869842 |
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