Seroprevalence to adeno‐associated virus type 6 in people with hemophilia B from a UK adult cohort

BACKGROUND: Gene therapy shows promise as a potential “cure” for hemophilia A and B. Adeno‐associated virus (AAV) vectors are the leading platform to deliver modified genetic code of factor VIII or IX to the liver effecting endogenous production. Patient exposure to wild‐type AAV leads to the format...

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Detalles Bibliográficos
Autores principales: Boyce, Sara, James, Izabela, Rangarajan, Savita, Curry, Nicola, Bagot, Catherine, Austin, Steven, Laffan, Mike, Mangles, Sarah, Chandrakumaran, Kandiah, Mundy, Carina
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2022
Materias:
Original Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9166283/
https://www.ncbi.nlm.nih.gov/pubmed/35677030
http://dx.doi.org/10.1002/rth2.12705

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9166283/
https://www.ncbi.nlm.nih.gov/pubmed/35677030
http://dx.doi.org/10.1002/rth2.12705

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