Gene Therapy for Mitochondrial Diseases: Current Status and Future Perspective

Mitochondrial diseases (MDs) are a group of severe genetic disorders caused by mutations in the nuclear or mitochondrial genome encoding proteins involved in the oxidative phosphorylation (OXPHOS) system. MDs have a wide range of symptoms, ranging from organ-specific to multisystemic dysfunctions, w...

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Detalles Bibliográficos
Autores principales: Di Donfrancesco, Alessia, Massaro, Giulia, Di Meo, Ivano, Tiranti, Valeria, Bottani, Emanuela, Brunetti, Dario
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9231068/
https://www.ncbi.nlm.nih.gov/pubmed/35745859
http://dx.doi.org/10.3390/pharmaceutics14061287

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9231068/
https://www.ncbi.nlm.nih.gov/pubmed/35745859
http://dx.doi.org/10.3390/pharmaceutics14061287

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