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Gene Therapy for Mitochondrial Diseases: Current Status and Future Perspective

Mitochondrial diseases (MDs) are a group of severe genetic disorders caused by mutations in the nuclear or mitochondrial genome encoding proteins involved in the oxidative phosphorylation (OXPHOS) system. MDs have a wide range of symptoms, ranging from organ-specific to multisystemic dysfunctions, w...

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Detalles Bibliográficos
Autores principales:	Di Donfrancesco, Alessia, Massaro, Giulia, Di Meo, Ivano, Tiranti, Valeria, Bottani, Emanuela, Brunetti, Dario
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9231068/ https://www.ncbi.nlm.nih.gov/pubmed/35745859 http://dx.doi.org/10.3390/pharmaceutics14061287

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