Cargando…

Current Outline of Exon Skipping Trials in Duchenne Muscular Dystrophy

Molecular treatments for Duchenne muscular dystrophy (DMD) are already in clinical practice. One particular means is exon skipping, an approach which has more than 15 years of background. There are several promising clinical trials based on earlier works. The aim is to be able to initiate the produc...

Descripción completa

Detalles Bibliográficos
Autores principales: Eser, Gökçe, Topaloğlu, Haluk
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9320322/
https://www.ncbi.nlm.nih.gov/pubmed/35886024
http://dx.doi.org/10.3390/genes13071241