An open-label pilot study of recombinant granulocyte-colony stimulating factor in Friedreich’s ataxia

Friedreich’s ataxia (FA) is an inherited progressive neurodegenerative disease for which there is no proven disease-modifying treatment. Here we perform an open‐label, pilot study of recombinant human granulocyte-colony stimulating factor (G-CSF) administration in seven people with FA (EudraCT: 2017...

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Detalles Bibliográficos
Autores principales: Kemp, Kevin C., Georgievskaya, Anastasia, Hares, Kelly, Redondo, Juliana, Bailey, Steven, Rice, Claire M., Scolding, Neil J., Metcalfe, Chris, Wilkins, Alastair
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Nature Publishing Group UK 2022
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9363409/
https://www.ncbi.nlm.nih.gov/pubmed/35945193
http://dx.doi.org/10.1038/s41467-022-31450-w

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9363409/
https://www.ncbi.nlm.nih.gov/pubmed/35945193
http://dx.doi.org/10.1038/s41467-022-31450-w

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