Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial

INTRODUCTION: The North Star Ambulatory Assessment (NSAA) tool is a key instrument for measuring clinical outcomes in patients with Duchenne muscular dystrophy (DMD). To gain a better understanding of the longitudinal utility of the NSAA, we evaluated NSAA data from a phase II trial of 120 patients...

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Detalles Bibliográficos
Autores principales: Muntoni, Francesco, Guglieri, Michela, Mah, Jean K., Wagner, Kathryn R., Brandsema, John F., Butterfield, Russell J., McDonald, Craig M., Mayhew, Anna G., Palmer, Jeffrey P., Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2022
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9397979/
https://www.ncbi.nlm.nih.gov/pubmed/35998119
http://dx.doi.org/10.1371/journal.pone.0272858

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9397979/
https://www.ncbi.nlm.nih.gov/pubmed/35998119
http://dx.doi.org/10.1371/journal.pone.0272858

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