Renoprotective Effect of Agalsidase Alfa: A Long-Term Follow-Up of Patients with Fabry Disease

Fabry disease is a rare lysosomal storage disorder caused by mutations in the GLA gene, which, without treatment, can cause significant renal dysfunction. We evaluated the effects of enzyme replacement therapy with agalsidase alfa on renal decline in patients with Fabry disease using data from the F...

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Detalles Bibliográficos
Autores principales: Cybulla, Markus, Nicholls, Kathleen, Feriozzi, Sandro, Linhart, Aleš, Torras, Joan, Vujkovac, Bojan, Botha, Jaco, Anagnostopoulou, Christina, West, Michael L.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9410255/
https://www.ncbi.nlm.nih.gov/pubmed/36013057
http://dx.doi.org/10.3390/jcm11164810

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9410255/
https://www.ncbi.nlm.nih.gov/pubmed/36013057
http://dx.doi.org/10.3390/jcm11164810

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